Turning the tide for rare disease

The transatlantic partnership advancing breakthrough science into innovative treatments for rare diseases

By CONTRIBUTOR

5 February 2025

RARE REV-inar

A blueprint to advance genomic medicine in Latin America

By CONTRIBUTOR

29 January 2025

Medical

Sepsis Research FEAT urges vigilance against sepsis this winter

By CONTRIBUTOR

28 January 2025

RARE News

Landmarks illuminate purple and blue for feeding tube awareness

By CONTRIBUTOR

28 January 2025

RARE caregiving

Considering caregiver value at JP Morgan

By CONTRIBUTOR

22 January 2025

Turning the tide for rare disease

Blood Sword by the Duncan Brothers: A mythical sword-wielding comedy to raise awareness of an underdiagnosed genetic condition

By CONTRIBUTOR

8 January 2025

Patient voice

“Having SDS shouldn’t hold you back, it shouldn’t define who you are.”

By CONTRIBUTOR

18 December 2024

Industry Insights

Looking backwards, looking forwards

By CONTRIBUTOR

11 December 2024

Turning the tide for rare disease

Bridging the gap: differing perceptions of generalised myasthenia disease burden

By CONTRIBUTOR

11 December 2024

Reviews

Here’s to baseball, hustlers and believing

By CONTRIBUTOR

9 December 2024

Turning the tide for rare disease

Becker muscular dystrophy patients find hope in building a community

By CONTRIBUTOR

4 December 2024

Turning the tide for rare disease

flok, pioneering patient-led research for inherited metabolic disorders (IMD) 

By CONTRIBUTOR

3 December 2024

Turning the tide for rare disease

Bridging the gap: health inequalities and rare diseases

By CONTRIBUTOR

29 November 2024

Turning the tide for rare disease

Rare disease—self-advocacy and getting needs met!

By CONTRIBUTOR

28 November 2024

Charity & advocacy

For George: The MVA Society

By CONTRIBUTOR

20 November 2024

Turning the tide for rare disease

Access to spinal muscular atrophy (SMA) treatment in Denmark: a success story of how persistence can win in the end

By CONTRIBUTOR

15 November 2024

Industry Insights

Real-world data in EAPs: makes sense for rare diseases

By CONTRIBUTOR

13 November 2024